Gene Therapy Startup Intellia Therapeutics

Country: USA | Funding: $1.2B (+)


  • Genome modifying technologies
  • Recombination and DNAAcronym for deoxyribonucleic acid, the hereditary material in humans and almost all other organisms. DNA can be found in the cell nucleus and contains the genetic instructions for the development, functioning, growth, and reproduction of all known organisms. Nearly every cell in a person’s body has the same DNA. repairCorrection of “misspelled” disease-driving DNA sequence using a CRISPR/Cas9-based gene editing therapy. technologies
  • RNA therapeutic technologies
  • Therapeutic delivery of nucleic acids or ribonucleoproteins – viral and chemical
  • Engineered immune cell technologies
  • Novel target identification

Intellia Therapeutics Announces FDA Clearance of Investigational New Drug (IND) Application for NTLA-2002, an In Vivo CRISPR-Based Investigational Therapy for the Treatment of Hereditary Angioedema (HAE) – Intellia Therapeutics (

Who are Intellia Therapeutics

Intellia Therapeutics is a biotechnology company founded in 2014 that focuses on developing gene editing therapies to treat genetic diseases. Based in Cambridge, Massachusetts, Intellia Therapeutics was founded by Jennifer Doudna, Emmanuelle Charpentier, and Rodger Novak, who were all pioneers in the development of the CRISPR/Cas9 gene-editing technology.

Intellia’s mission is to harness the power of CRISPR/Cas9 to develop curative treatments for genetic diseases. The company’s approach involves using CRISPR/Cas9 to edit the genetic code of patients with genetic diseases, correcting the underlying genetic mutations that cause the disease. Intellia believes that gene editing has the potential to provide a one-time, curative treatment for many genetic diseases, including inherited diseases such as sickle cell anemia, beta-thalassemia, and cystic fibrosis.

One of the key advantages of Intellia’s approach is its precision. By using CRISPR/Cas9, Intellia can target specific genes with incredible accuracy, minimizing the risk of off-target effects. This precision is essential for developing safe and effective gene editing therapies.

Intellia is also working to develop its gene editing platform for use in other applications, such as agricultural biotechnology and industrial biotechnology. The company has partnered with several leading companies in these fields to explore the potential of its gene editing technology.

Intellia’s lead program is focused on developing a curative treatment for transthyretin amyloidosis (ATTR), a rare genetic disease that causes the buildup of abnormal proteins in the body’s tissues and organs, leading to organ damage and failure. Intellia’s therapy involves using CRISPR/Cas9 to edit the DNA in liver cells, the source of the abnormal protein, to reduce or eliminate the production of the abnormal protein.

Intellia has also partnered with Regeneron Pharmaceuticals to develop gene editing therapies for a range of genetic diseases, including hemophilia and lysosomal storage disorders. The company has also partnered with Novartis to develop gene-editing therapies for cancer and autoimmune diseases.

Intellia’s innovative approach to gene editing has earned the company numerous awards and recognition, including being named a Technology Pioneer by the World Economic Forum and being named to the MIT Technology Review’s 50 Smartest Companies list. The company is well-funded, with backing from top venture capital firms and strategic partnerships with leading pharmaceutical and biotech companies.

Intellia Therapeutics is a leading biotechnology company focused on developing gene editing therapies for genetic diseases. Using the precision and power of CRISPR/Cas9, Intellia aims to provide one-time, curative treatments for a range of genetic diseases, offering new hope for patients and their families. With a strong pipeline of programs and strategic partnerships, Intellia is poised to make a significant impact in the field of gene editing and transform the lives of patients with genetic diseases.

How does Intellia market its business?

Intellia Therapeutics, as a biotechnology company, has a unique marketing approach that differs from traditional consumer-based marketing. Instead of marketing products directly to consumers, Intellia markets its business to investors, potential partners, and the scientific community.

One of the key ways Intellia markets its business is through scientific publications and presentations at industry conferences. By presenting its research and findings in prestigious scientific journals and conferences, Intellia can establish its expertise in the field of gene editing and gain credibility with potential investors and partners.

Intellia also uses social media and its website to share news and updates about its progress and achievements. They regularly post updates about their clinical trials, partnerships, and scientific breakthroughs. This helps to keep investors, partners, and the scientific community informed and engaged with the company’s progress.

In addition to these marketing efforts, Intellia has also participated in various media interviews, including television and print media, to increase awareness of the potential of gene editing and its unique approach to developing gene therapies.

Intellia also relies on its strategic partnerships with leading pharmaceutical and biotech companies to help promote its business. By partnering with established industry players, Intellia gains access to its network and resources, which can help to advance the development and commercialization of its gene editing therapies.


Intellia Therapeutics markets its business primarily through scientific publications, industry conferences, social media, and partnerships with leading pharmaceutical and biotech companies. By focusing on establishing credibility and awareness within the scientific and investment communities, Intellia is able to attract funding and partnerships that can help to advance the development of their innovative gene editing therapies.


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